Enrolling by invitationNCT04628585
Long-term Follow-up of Subjects with Sickle Cell Disease Treated with Ex Vivo Gene Therapy
Studying Sickle cell disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Genetix Biotherapeutics Inc.
- Principal Investigator
- Anjulika Chawla, MD, MD, MPHbluebird bio, Inc.
- Intervention
- Safety and efficacy assessments(other)
- Enrollment
- 85 enrolled
- Eligibility
- 2-53 years · All sexes
- Timeline
- 2020 – 2038
Study locations (16)
- University of Alabama, Birmingham, Alabama, United States
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- Children's Healthcare of Atlanta, Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Warren Grant Magnuson Clinical Center, Bethesda, Maryland, United States
- University of Minnesota Masonic Children's Hospital, Minneapolis, Minnesota, United States
- Hackensack University Medical Center, Hackensack, New Jersey, United States
- Cohen Children's Medical Center, New Hyde Park, New York, United States
- Columbia University Medical Center, New York, New York, United States
- The University of North Carolina, Chapel Hill, North Carolina, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Medical University of South Carolina, Charleston, South Carolina, United States
- Baylor College of Medicine, Houston, Texas, United States
- Virginia Commonwealth University, Richmond, Virginia, United States
- +1 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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