CompletedPhase 2NCT04336826
A Study to Evaluate the Safety and Pharmacokinetics of Ataluren in Participants From ≥6 Months to <2 Years of Age With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- PTC Therapeutics
- Principal Investigator
- Vinay PenematsaPTC Therapeutics, Inc.
- Intervention
- Ataluren(drug)
- Enrollment
- 6 enrolled
- Eligibility
- 2 years · MALE
- Timeline
- 2021 – 2023
Study locations (1)
- Rare Disease Research, LLC, Atlanta, Georgia, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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