Active, not recruitingPHASE1, PHASE2NCT04120493
Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington's Disease
Studying Huntington's Disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- UniQure Biopharma B.V.
- Principal Investigator
- David H. Margolin, MD, PhDuniQure, Inc.
- Intervention
- intra-striatal rAAV5-miHTT(genetic)
- Enrollment
- 43 enrolled
- Eligibility
- 25-65 years · All sexes
- Timeline
- 2019 – 2029
Study locations (12)
- University of Alabama at Birmingham, Birmingham, Alabama, United States
- University of Arizona (Surgical Site Only), Tucson, Arizona, United States
- University of California, San Francisco, San Francisco, California, United States
- CenExel Rocky Mountain Clinical Research, Englewood, Colorado, United States
- Rush University Medical Center, Chicago, Illinois, United States
- Johns Hopkins University, Baltimore, Maryland, United States
- University of Michigan Department of Neurology, Ann Arbor, Michigan, United States
- Ohio State University, Columbus, Ohio, United States
- Vanderbilt University Medical Center, Nashville, Tennessee, United States
- The University of Texas, Houston, Texas, United States
- Virginia Commonwealth University VCU School of Medicine, Department of Neurology, Richmond, Virginia, United States
- University of Washington Medical Center, Seattle, Washington, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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