WithdrawnPhase 1NCT03825783

A Gene Therapy Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I

Studying Leukocyte adhesion deficiency

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Key facts

Sponsor
Rocket Pharmaceuticals Inc.
Principal Investigator
Julián Sevilla Navarro, MD, PhD
Hospital Infantil Universitario Niño Jesús (HIUNJ)
Intervention
RP-L201(biological)
Eligibility
All sexes
Timeline
20192021

Study locations (1)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT03825783 on ClinicalTrials.gov

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