Active, not recruitingNCT06282432
Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I)
Studying Leukocyte adhesion deficiency
Last synced from ClinicalTrials.gov
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Report missing dataKey facts
- Sponsor
- Rocket Pharmaceuticals Inc.
- Principal Investigator
- Donald Kohn, MD, D.D.SUniversity of California, Los Angeles
- Enrollment
- 9 enrolled
- Eligibility
- All sexes
- Timeline
- 2022 – 2036
Study locations (3)
- University of California, Los Angeles (UCLA), Los Angeles, California, United States
- Hospital Infantil Universitario Niño Jesús, Madrid, Spain
- University College London Great Ormond Street Institute of Child Health (GOSH), London, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06282432 on ClinicalTrials.gov