CompletedPhase 2NCT03796637
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Ataluren
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- PTC Therapeutics
- Principal Investigator
- Francesco Bibbiani, MDPTC Therapeutics, Inc.
- Intervention
- Ataluren(drug)
- Enrollment
- 6 enrolled
- Eligibility
- MALE
- Timeline
- 2019 – 2019
Study locations (1)
- University of California, Los Angeles (UCLA), Los Angeles, California, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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