CompletedPhase 2NCT03648827
A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- PTC Therapeutics
- Principal Investigator
- Francesco Bibbiani, MDPTC Therapeutics, Inc.
- Intervention
- Ataluren(drug)
- Enrollment
- 20 enrolled
- Eligibility
- 2-7 years · MALE
- Timeline
- 2018 – 2020
Study locations (9)
- Phoenix Childrens Hospital, Phoenix, Arizona, United States
- University of California, Los Angeles (UCLA), Los Angeles, California, United States
- University of California (UC) Davis Medical Center, Sacramento, California, United States
- University of Kansas Medical Center, Kansas City, Kansas, United States
- University of Minnesota, Minneapolis, Minnesota, United States
- Columbia University College of Physicians & Surgeons, New York, New York, United States
- Texas Children's Hospital, Houston, Texas, United States
- University of Texas Heath Science Center at San Antonio, San Antonio, Texas, United States
- Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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