UnknownNot applicableNCT03351868

FANCA Gene Transfer for Fanconi Anemia Using a High-safety, High-efficiency, Self-inactivating Lentiviral Vector

Studying Fanconi anemia

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Key facts

Sponsor
Shenzhen Geno-Immune Medical Institute
Principal Investigator
Lung-Ji Chang, Ph.D
Shenzhen Geno-Immune Medical Institute
Intervention
Gene-modified autologous stem cells(genetic)
Enrollment
10 enrolled
Eligibility
2-20 years · All sexes
Timeline
20172021

Study locations (3)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT03351868 on ClinicalTrials.gov

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