Active, not recruitingPhase 2NCT04069533
Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A
Studying Fanconi anemia
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Rocket Pharmaceuticals Inc.
- Principal Investigator
- Julián Sevilla Navarro, MD, PhDHospital Infantil Universitario Niño Jesús (HIUNJ)
- Intervention
- RP-L102(biological)
- Enrollment
- 7 enrolled
- Eligibility
- 1-17 years · All sexes
- Timeline
- 2019 – 2025
Study locations (2)
- Hospital Infantil Universitario Niño Jesús (HIUNJ), Madrid, Spain
- University College London Great Ormond Street Institute of Child Health (GOSH), London, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04069533 on ClinicalTrials.govOther trials for Fanconi anemia
Additional recruiting or active studies for the same condition.
- RECRUITINGNANCT06744283Experience and Management of Cancer Screening-Related Anxiety in Fanconi AnemiaNational Cancer Institute (NCI)
- RECRUITINGPHASE1, PHASE2NCT06648096Afatinib in Patients with Fanconi Anemia (FA) and Advanced Head and Neck Squamous Cell Carcinoma (HNSCC)Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau
- RECRUITINGNANCT05687149Defining the Natural History of Squamous Cell Carcinoma in Fanconi AnemiaNational Cancer Institute (NCI)
- RECRUITINGNANCT05973656Role of Acetaldehyde in the Development of Oral CancerMasonic Cancer Center, University of Minnesota
- RECRUITINGPHASE1, PHASE2NCT04784052Depleted Donor Stem Cell Transplant in Children and Adults With Fanconi Anemia After Being Conditioned With a Regimen Containing BriquilimabPorteus, Matthew, MD
- ACTIVE NOT RECRUITINGPHASE2NCT04248439Gene Therapy for Fanconi Anemia, Complementation Group ARocket Pharmaceuticals Inc.
- ACTIVE NOT RECRUITINGNANCT04437771Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene TherapyRocket Pharmaceuticals Inc.
- RECRUITINGPHASE2NCT03579875Alpha/Beta TCD HCT in Patients With Inherited BMF DisordersMasonic Cancer Center, University of Minnesota