Active, not recruitingPhase 1NCT03282656
Gene Transfer for Sickle Cell Disease
Studying Sickle cell disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- David Williams
- Principal Investigator
- Erica Esrick, MD, MD, MPHBoston Children's Hospital
- Intervention
- single infusion of autologous bone marrow derived CD34+ HSC cells transduced with the lentiviral vector containing a short-hairpin RNA targeting BCL11a(biological)
- Enrollment
- 10 enrolled
- Eligibility
- 3-40 years · All sexes
- Timeline
- 2018 – 2026
Study locations (2)
- UCLA - Mattel Children's Hospital, Los Angeles, California, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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