TerminatedPhase 1NCT02986698

In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM)

Studying Alpha-thalassemia

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Key facts

Sponsor
University of California, San Francisco
Principal Investigator
Tippi Mackenzie, MD
University of California, San Francisco
Intervention
in utero hematopoietic stem cell transplantation(biological)
Enrollment
6 enrolled
Eligibility
All sexes
Timeline
20172024

Study locations (1)

Collaborators

California Institute for Regenerative Medicine (CIRM)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT02986698 on ClinicalTrials.gov

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