International Registry of Patients With Alpha Thalassemia

Key facts

Sponsor

University of California, San Francisco

Principal Investigator

Tippi C MacKenzie, MD

University of California, San Francisco

Enrollment

500 enrolled

Eligibility

All sexes

Timeline

2017 – 2037

Study locations (1)

• University of California San Francisco, San Francisco, California, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Alpha-thalassemia

Additional recruiting or active studies for the same condition.

• RECRUITINGNCT06591936
  Genetic Profile of Alpha Thalassemia Children at Sohag University Hospital .
  Sohag University
• RECRUITINGNANCT06539169
  FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
  xCures
• RECRUITINGEARLY PHASE1NCT06107400
  Safety and Efficacy of RM-004 Cells for Hemoglobin H-Constant Spring Disease
  The 923rd Hospital of Joint Logistics Support Force of People's Liberation Army
• RECRUITINGPHASE2NCT05664737
  A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia
  Bristol-Myers Squibb
• ACTIVE NOT RECRUITINGPHASE3NCT04770753
  A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)
  Agios Pharmaceuticals, Inc.
• ACTIVE NOT RECRUITINGPHASE3NCT04770779
  A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
  Agios Pharmaceuticals, Inc.
• ACTIVE NOT RECRUITINGNANCT02692872
  Screening for Alpha Thalassemia in Healthy Volunteers
  National Institute of Allergy and Infectious Diseases (NIAID)

See all trials for Alpha-thalassemia →