CompletedPHASE1, PHASE2NCT02725580
Gene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 (vLINCL6) Disease
Studying Neuronal ceroid lipofuscinosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Emily de los Reyes
- Principal Investigator
- Emily de los Reyes, MDNationwide Children's Hospital
- Intervention
- AT-GTX-501(genetic)
- Enrollment
- 13 enrolled
- Eligibility
- 1 years · All sexes
- Timeline
- 2016 – 2024
Study locations (1)
- Nationwide Children's Hosptial, Columbus, Ohio, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT02725580 on ClinicalTrials.govOther trials for Neuronal ceroid lipofuscinosis
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