Clinical trials for Neuronal ceroid lipofuscinosis
4 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGNCT06844877Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic StrategiesIRCCS Fondazione Stella Maris · PI: Filippo M Santorelli, Dr.
- RECRUITINGN/ANCT04613089Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD DatabaseUniversitätsklinikum Hamburg-Eppendorf · PI: Angela Schulz, MD, PhD
- ACTIVE NOT RECRUITINGNCT04098211Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency PatientsChildren's Hospital of Orange County
- RECRUITINGN/ANCT03307304Investigations of Juvenile Neuronal Ceroid LipofuscinosisEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) · PI: An N Dang Do, M.D.