CompletedPHASE1, PHASE2NCT02354781
Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Jerry R. Mendell
- Principal Investigator
- Jerry R Mendell, MDDirector, Center for Gene Therapy, Nationwide Children's Hospital
- Intervention
- rAAV1.CMV.huFollistin344(biological)
- Enrollment
- 3 enrolled
- Eligibility
- 7 years · MALE
- Timeline
- 2015 – 2017
Study locations (1)
- Nationwide Children's Hospital, Columbus, Ohio, United States
Collaborators
Duchenne Alliance · Milo Therapeutics
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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