CompletedPHASE1, PHASE2NCT02247843
Stem Cell Gene Therapy for Sickle Cell Disease
Studying Sickle cell anemia
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Donald B. Kohn, M.D.
- Principal Investigator
- Donald Kohn, MDUniversity of California, Los Angeles
- Intervention
- βAS3-FB vector transduced peripheral blood CD34+ cells(biological)
- Enrollment
- 4 target
- Eligibility
- 18 years · All sexes
- Timeline
- 2014 – 2025
Study locations (1)
- University of California, Los Angeles (UCLA), Los Angeles, California, United States
Collaborators
California Institute for Regenerative Medicine (CIRM)
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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