CompletedPHASE1, PHASE2NCT01496040
Clinical Gene Therapy Protocol for the Treatment of Retinal Dystrophy Caused by Defects in RPE65
Studying Leber congenital amaurosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Nantes University Hospital
- Principal Investigator
- Michel WEBER, ProfessorNantes University Hospital
- Intervention
- rAAV2/4.hRPE65(drug)
- Enrollment
- 9 target
- Eligibility
- 6-50 years · All sexes
- Timeline
- 2011 – 2014
Study locations (1)
- CHU Nantes, Nantes, France
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT01496040 on ClinicalTrials.govOther trials for Leber congenital amaurosis
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- ACTIVE NOT RECRUITINGEARLY PHASE1NCT06088992Leber Congenital Amaurosis Inherited Blindness of Gene Therapy Trial(LIGHT)Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
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- ACTIVE NOT RECRUITINGPHASE3NCT00999609Safety and Efficacy Study in Subjects With Leber Congenital AmaurosisSpark Therapeutics, Inc.
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