Clinical trials for Leber congenital amaurosis
7 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPhase 3NCT06891443Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)Laboratoires Thea
- RECRUITINGPHASE1, PHASE2NCT05906953Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)HuidaGene Therapeutics Co., Ltd. · PI: Study Director
- ACTIVE NOT RECRUITINGEarly Phase 1NCT06088992Leber Congenital Amaurosis Inherited Blindness of Gene Therapy Trial(LIGHT)Xinhua Hospital, Shanghai Jiao Tong University School of Medicine · PI: Peiquan Zhao
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT03920007Study of Subretinally Injected ATSN-101 Administered in Patients With Leber Congenital Amaurosis Caused by Biallelic Mutations in GUCY2DAtsena Therapeutics Inc.
- ACTIVE NOT RECRUITINGPHASE2, PHASE3NCT03913143A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)ProQR Therapeutics · PI: ProQR Medical Monitor
- ACTIVE NOT RECRUITINGPhase 3NCT00999609Safety and Efficacy Study in Subjects With Leber Congenital AmaurosisSpark Therapeutics, Inc. · PI: Albert M Maguire, MD
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT01208389Phase 1 Follow-on Study of AAV2-hRPE65v2 Vector in Subjects With Leber Congenital Amaurosis (LCA) 2Spark Therapeutics, Inc. · PI: Clinical Director