CompletedPHASE1, PHASE2NCT01414985
AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis
Studying Neuronal ceroid lipofuscinosis
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Weill Medical College of Cornell University
- Principal Investigator
- Ronald Crystal, MDWeill Medical College of Cornell University
- Intervention
- AAVrh.10CUCLN2(biological)
- Enrollment
- 8 enrolled
- Eligibility
- 3-18 years · All sexes
- Timeline
- 2010 – 2017
Study locations (1)
- Weill Cornell Medical College, New York, New York, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT01414985 on ClinicalTrials.govOther trials for Neuronal ceroid lipofuscinosis
Additional recruiting or active studies for the same condition.
- RECRUITINGNCT06844877Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic StrategiesIRCCS Fondazione Stella Maris
- RECRUITINGNANCT04613089Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD DatabaseUniversitätsklinikum Hamburg-Eppendorf
- ACTIVE NOT RECRUITINGNCT04098211Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency PatientsChildren's Hospital of Orange County
- RECRUITINGNANCT03307304Investigations of Juvenile Neuronal Ceroid LipofuscinosisEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)