UnknownNCT01385917
Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Genethon
- Principal Investigator
- Laurent SERVAIS, MDMyology Institute
- Enrollment
- 45 enrolled
- Eligibility
- 12-20 years · MALE
- Timeline
- 2011 – 2018
Study locations (2)
- Myology Institute, Paris, France
- Great ormond Street Hospital & University College London Hospital, London, United Kingdom
Collaborators
Institute of Myology
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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