CompletedPHASE1, PHASE2NCT01362595
Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia
Studying Diamond-Blackfan anemia
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Northwell Health
- Principal Investigator
- Adrianna Vlachos, MDFeinstein Institutes for Medical Research; Cohen Children's Medical Center
- Intervention
- leucine(drug)
- Enrollment
- 55 enrolled
- Eligibility
- 2 years · All sexes
- Timeline
- 2013 – 2020
Study locations (11)
- Phoenix Children's Hospital, Phoenix, Arizona, United States
- Stanford University Medical Center, Palo Alto, California, United States
- Riley Hospital for Children, Indianapolis, Indiana, United States
- University of Louisville, Louisville, Kentucky, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- University of Michigan C.S. Mott Children's Hospital, Ann Arbor, Michigan, United States
- University of Missouri-Columbia Women's and Children's Hospital, Columbia, Missouri, United States
- Children's Specialty Center of Nevada, Las Vegas, Nevada, United States
- Cohen Children's Medical Center of New York, New Hyde Park, New York, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- UT Southwestern Medical Center, Dallas, Texas, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT01362595 on ClinicalTrials.govOther trials for Diamond-Blackfan anemia
Additional recruiting or active studies for the same condition.
- RECRUITINGPHASE1NCT07476183Assessing the Safety, Tolerability, and Efficacy of APR-2020 in Pediatric and Adolescent Subjects With RPS19 Deficient Diamond-Blackfan AnemiaApriligen, Inc.
- RECRUITINGNANCT07186179Mobilization of CD34+ Peripheral Blood Stem Cells in Patients With Diamond Blackfan Anemia Syndrome (DBAS)Northwell Health
- RECRUITINGPHASE2NCT03214354Nonmyeloablative Stem Cell Transplant in Children with Sickle Cell Disease and a Major ABO-Incompatible Matched Sibling DonorUniversity of Calgary
- RECRUITINGNCT02720679Investigation of the Genetics of Hematologic DiseasesSt. Jude Children's Research Hospital
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT01966367CD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell TransplantationDiane George
- RECRUITINGNCT00106015Diamond Blackfan Anemia Registry (DBAR)Northwell Health
- RECRUITINGNANCT00027274Cancer in Inherited Bone Marrow Failure SyndromesNational Cancer Institute (NCI)