RecruitingPhase 1NCT07476183
Assessing the Safety, Tolerability, and Efficacy of APR-2020 in Pediatric and Adolescent Subjects With RPS19 Deficient Diamond-Blackfan Anemia
Studying Diamond-Blackfan anemia
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Apriligen, Inc.
- Intervention
- APR-2020(biological)
- Enrollment
- 4 enrolled
- Eligibility
- 2-18 years · All sexes
- Timeline
- 2026 – 2028
Study locations (2)
- Stanford University - Stanford Children's Health, Stanford, California, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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