CompletedPhase 2NCT00264888
Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy
Studying Duchenne muscular dystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- PTC Therapeutics
- Principal Investigator
- Richard Finkel, MDChildren's Hospital of Philadelphia
- Intervention
- PTC124(drug)
- Enrollment
- 38 enrolled
- Eligibility
- 5 years · MALE
- Timeline
- 2005 – 2007
Study locations (3)
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- University of Utah, Salt Lake City, Utah, United States
Collaborators
Muscular Dystrophy Association
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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