Rare disease news

FDA approvals, research breakthroughs, clinical trials, and advocacy updates

Curated and summarized by AI for patients and caregivers

🔍
AllDrug approvalsClinical trialsResearchGrants & fundingAdvocacy & policyPipeline
Show:All newsBreaking onlyImportant & breaking
Date:7 days30 days90 daysAll time

1 article from the last 30 days matching "life stages"

NewsRSS2 days ago

At 12, I Couldn’t Gain Weight With Pompe Disease, but at 35, I Struggle to Lose It

A person with Pompe disease shares how their weight challenges changed over time. As a child, they couldn't gain weight and stayed at 60 pounds. Now as an adult at 35 years old, they face the opposite problem and struggle to lose weight. This shows how Pompe disease can affect the body differently at different life stages.

WHY IT MATTERSThis personal account highlights how Pompe disease's metabolic effects evolve with age and treatment, which can help newly diagnosed patients and families understand what to expect as they grow older.
Good to knowPompe diseaseRead →

Get personalized rare disease news

Follow your conditions to see news about the diseases that matter to you — FDA approvals, trial openings, and research breakthroughs.

Create free account →Browse diseases