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2 articles from the last 30 days matching "Amyotrophic Lateral Sclerosis"

Clinical trialRSSMay 4

Dazucorilant shows significant survival benefit in Phase 2 ALS trial

A new experimental drug called dazucorilant helped people with ALS live longer when given at a higher dose, according to a Phase 2 clinical trial. While the trial didn't fully meet all its main goals, the survival benefit was significant enough to be noteworthy. This suggests the drug may have promise for treating ALS, a disease that affects nerve cells controlling muscles.

WHY IT MATTERSIf dazucorilant advances to Phase 3 testing, ALS patients may have access to a new treatment option that could extend survival, which is critical since current ALS therapies have limited effectiveness.
👁 Watch this spaceamyotrophic lateral sclerosis
Clinical trialRSSApr 28

RAG-17 shows promise in SOD1-ALS trial, reducing damage markers

Scientists are testing a new drug called RAG-17 for people with a specific type of ALS (a disease that weakens muscles over time) caused by a SOD1 gene mutation. Early results show the drug was safe at different doses and made important disease markers improve. This is early-stage testing, but it's a promising first step.

WHY IT MATTERSIf you have SOD1-ALS, this is one of the first treatments specifically designed for your genetic form of the disease, and early signs suggest it may slow the damage happening in your body.
💬 Ask your doctoramyotrophic lateral sclerosis (SOD1-ALS)

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