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5 articles from the last 30 days matching "muscular dystrophy"

AdvocacyRSS5 days ago

Patient-led group launches network of clinics to improve LGMD care

A patient-led nonprofit called The Speak Foundation has created a network of specialized clinics called LGMD Centers of Excellence to help people with limb-girdle muscular dystrophy (LGMD), a rare muscle disease. This new network aims to solve a major problem: patients with LGMD have had trouble getting consistent care and doctors have struggled to develop new treatments because the patient population is very small and spread out.

WHY IT MATTERSThis coordinated clinic network could help LGMD patients access specialized care in one place and speed up the development of new treatments by making it easier for researchers to find and study patients.
Good to knowLimb-girdle muscular dystrophy (LGMD)Read →
AdvocacyRSS5 days ago

Collaboration aims to improve design of FSHD clinical trials

Three organizations that work with facioscapulohumeral muscular dystrophy (FSHD) patients are joining together to make clinical trials better. FSHD is a rare muscle disease that causes weakness in the face, shoulders, and upper arms. This partnership wants to improve how these trials are designed so they can test new treatments more effectively.

WHY IT MATTERSBetter-designed clinical trials mean faster progress toward treatments for FSHD, and patient input through the FSHD Society ensures trials are structured in ways that actually work for people living with the disease.
Good to knowFacioscapulohumeral muscular dystrophyRead →
AdvocacyRSS5 days ago

To me, a wheelchair is a symbol of improved function, not disability

A person with a muscular dystrophy explains how using a wheelchair has improved their quality of life and ability to participate in daily activities. Rather than viewing the wheelchair as a symbol of disability, they see it as a tool that gives them more independence and function. The article challenges common misconceptions about wheelchairs and disability.

WHY IT MATTERSThis perspective piece helps patients with muscular dystrophy and other mobility conditions understand that mobility aids like wheelchairs can expand independence rather than limit it, which may help reduce stigma and encourage earlier adoption of helpful devices.
Good to knowMuscular DystrophyRead →
AdvocacyRSS5 days ago

Navigating disability benefits for muscular dystrophy

When muscular dystrophy makes it hard to work, you may qualify for disability benefits that provide money and health insurance. This article explains how to navigate the process of getting these public benefits so you don't lose financial stability. Understanding your options can help you manage living with MD while keeping some independence.

WHY IT MATTERSPeople with muscular dystrophy who can no longer work need to know how to access disability benefits and medical coverage to avoid financial hardship during disease progression.
💬 Ask your doctorMuscular DystrophyRead →
AdvocacyRSS5 days ago

I won’t apologize for having 3 children with Duchenne MD

A mother of seven children shares her story about having three sons with Duchenne muscular dystrophy, a serious genetic muscle disease. She discusses her decision to have children despite knowing the genetic risks and explains why she doesn't regret her family planning choices. The article focuses on her perspective as both a caregiver and parent navigating life with this condition.

WHY IT MATTERSThis personal narrative highlights the lived experience and decision-making process for families with Duchenne muscular dystrophy, offering perspective on genetic counseling, family planning, and the emotional aspects of raising multiple children with the same rare disease.
Good to knowDuchenne muscular dystrophyRead →

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