NewsAMERICAN JOURNAL OF HEMATOLOGYMonday, January 5, 2026 · January 5, 2026
Iptacopan for Immune Thrombocytopenia and Cold Agglutinin Disease: A Global Phase 2 Basket Clinical Trial.
WHY IT MATTERS
Recent peer-reviewed research on Immune thrombocytopenia that may be relevant for patients and caregivers.
Iptacopan is a first-in-class, oral, selective inhibitor of complement factor B that has demonstrated positive efficacy across several complement-driven diseases. Here we evaluate the efficacy and safety of iptacopan monotherapy in adult patients with primary immune thrombocytopenia (ITP) and primar...
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