NewsTHER ADV RARE DISTuesday, December 1, 2026 · -220 days ago
Could an outcome-based agreement be operationalized using real-world data from the Canadian Neuromuscular Disease Registry? Perspectives from an expert-led assessment in spinal muscular atrophy
WHY IT MATTERS
Recent peer-reviewed research relevant to rare disease diagnosis or treatment.
Published in Ther Adv Rare Dis. Mitha A et al.
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