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NewsMOL THER NUCLEIC ACIDSTuesday, June 16, 2026 · -52 days ago

The post-pandemic pivot: mRNA therapeutics enter the chronic rare disease arena

WHY IT MATTERS

Recent peer-reviewed research relevant to rare disease diagnosis or treatment.

Published in Mol Ther Nucleic Acids. Giangrande PH et al.

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Read the original at Mol Ther Nucleic Acids
ResearchPubMed

Related conditions

Ornithine transcarbamylase deficiencyMethylmalonic acidemia due to methylmalonyl-CoA epimerase deficiencyMethylmalonic acidemia with homocystinuriaMethylmalonic acidemia with homocystinuria type cblFPropionic acidemia

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