NewsJOURNAL OF THROMBOSIS AND HAEMOSTASIS : JTHSaturday, March 7, 2026 · March 7, 2026
Overview of gene therapy for hemophilia: questions and answers to navigate the innovation.
WHY IT MATTERS
Recent peer-reviewed research on Hemophilia A that may be relevant for patients and caregivers.
Hemophilia is a rare inherited bleeding disorder affecting approximately 1.1 million individuals worldwide, characterized by deficiency in clotting factor (F)VIII (hemophilia A) or FIX (hemophilia B). Despite advances in prophylactic factor replacement therapy and nonfactor treatments, persons with ...
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