NewsNATURE BIOTECHNOLOGYTuesday, February 17, 2026 · February 17, 2026
Engineering a photoactivatable A-to-I RNA base editor for gene therapy in vivo.
WHY IT MATTERS
Recent peer-reviewed research on Hemophilia B that may be relevant for patients and caregivers.
Tunable and reversible regulation of exogenous and endogenous gene expression would be useful for improving the safety and efficacy of gene therapy. Current chemically inducible systems are limited by the rapid diffusion and extended metabolism of small molecules, and associated side effects. Here w...
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