NewsTHE NEW ENGLAND JOURNAL OF MEDICINEWednesday, January 28, 2026 · January 28, 2026
Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B.
WHY IT MATTERS
Recent peer-reviewed research on Hemophilia B that may be relevant for patients and caregivers.
Prophylactic treatment for hemophilia B necessitates lifelong, regular intravenous factor IX infusions. Gene therapy offers the possibility of a single-dose treatment that produces durable endogenous factor IX expression and disease control. Etranacogene dezaparvovec comprises an adeno-associated vi...
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