NewsATHEROSCLEROSISFriday, February 6, 2026 · February 6, 2026
Evinacumab in patients aged 5-17 years with homozygous familial hypercholesterolemia.
WHY IT MATTERS
Recent peer-reviewed research on Homozygous familial hypercholesterolemia that may be relevant for patients and caregivers.
Children and adolescents with homozygous familial hypercholesterolemia (HoFH) routinely require advanced lipid-lowering therapies (LLTs). We assess the long-term efficacy and safety of evinacumab, a novel LLT, in children and adolescents with HoFH. Study 17100 (NCT04233918) was a phase 3, single-arm...
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