NewsAUTOPHAGYWednesday, March 25, 2026 · March 25, 2026
Muscle meets Lysosomes: emerging strategies in muscular dystrophy.
WHY IT MATTERS
Recent peer-reviewed research on Duchenne muscular dystrophy that may be relevant for patients and caregivers.
Duchenne muscular dystrophy (DMD) is caused by the loss of DMD (dystrophin), leading to sarcolemmal fragility and progressive muscle degeneration. Although adeno-associated viral (AAV) microdystrophin ( µDMD ) therapies have advanced clinically, their benefits remain partial, highlighting the n...
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