NewsJOURNAL OF BLOOD MEDICINETuesday, March 3, 2026 · March 3, 2026
Current Status of Clinical Gene Therapy for Hemophilia and Globin Disorders.
WHY IT MATTERS
Recent peer-reviewed research on Hemophilia B that may be relevant for patients and caregivers.
In the last few years, gene therapy, holding the promise for long-term disease correction through a one-time treatment, has transitioned from experimental research to approved medicine. Several gene therapies are now available for congenital blood disorders, notably for hemophilia and hemoglobinopat...
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