NewsTHROMBOSIS RESEARCHSaturday, April 11, 2026 · April 11, 2026
Optimized AAVrh10 and Factor 9 vectors demonstrate improved phenotypic rescue in hemophilia B mice.
WHY IT MATTERS
Recent peer-reviewed research on Hemophilia B that may be relevant for patients and caregivers.
Hemophilia B is an X-linked bleeding disorder caused by a functional deficiency of coagulation factor IX (FIX). Adeno-associated virus (AAV) mediated gene therapy based on vector serotypes 5 and 8, has shown promising clinical outcomes. Nonetheless, a high prevalence of neutralizing antibodies in th...
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