NewsCURRENT OPINION IN PEDIATRICSWednesday, April 1, 2026 · April 1, 2026
Treatment advances for Duchenne muscular dystrophy.
WHY IT MATTERS
Recent peer-reviewed research on Duchenne muscular dystrophy that may be relevant for patients and caregivers.
Duchenne muscular dystrophy (DMD) is a severe X-linked muscle wasting disease with childhood onset that leads to loss of ambulation in the teenage years and mortality in the second or third decade of life. Prior to 10 years ago, disease-modifying pharmacologic intervention was limited to glucocortic...
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