Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

6 matching diseasesClear search ×

Persistent hyperplastic primary vitreous

Non-syndromic congenital retinal non-attachment · PFVS

ORPHA:91495

Fetal encasement syndrome

ORPHA:465824

Fetal valproate spectrum disorder

Fetal valproic acid syndrome · Valproic acid embryopathy

ORPHA:1906

Microcornea-posterior megalolenticonus-persistent fetal vasculature-coloboma syndrome

MPPC syndrome

ORPHA:231736

Persistent Müllerian duct syndrome

PMDS · Persistent Müllerian derivatives

ORPHA:2856

Robinow syndrome

Acral dysostosis with facial and genital abnormalities · Fetal face syndrome

ORPHA:97360