Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

9 matching diseasesClear search ×

GM1 gangliosidosis type 1

Infantile GM1 gangliosidosis · Norman-Landing disease

ORPHA:79255

Erythema palmare hereditarium

Lane disease · Red palms disease

ORPHA:231031

Familial LCAT deficiency

Complete LCAT deficiency · FLD

ORPHA:79293

GM1 gangliosidosis

Beta-galactosidase-1 deficiency · GLB1 deficiency

ORPHA:354

Histoplasmosis

Darling disease

ORPHA:390

Lafora disease

EPM2 · PME type 2

ORPHA:501

Norrie disease

Atrophia bulborum hereditaria · Episkopi blindness

ORPHA:649

Pontocerebellar hypoplasia type 1

Norman disease · PCH1

ORPHA:2254

Wolman disease

ORPHA:75233