Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

5 matching diseasesClear search ×

McLeod neuroacanthocytosis syndrome

MLS · X-linked McLeod syndrome

ORPHA:59306

Mantle cell lymphoma

LCM · MCL

ORPHA:52416

O'Sullivan-McLeod syndrome

ORPHA:99965

OBSOLETE: McLain-Dekaban syndrome

OBSOLETE: Intellectual disability-coloboma-slimness syndrome

ORPHA:2474

Acute mast cell leukemia

Acute MCL

ORPHA:566393