Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

7 matching diseasesClear search ×

Odontoleukodystrophy

Dentoleukoencephalopathy · Leukodystrophy with oligodontia

ORPHA:77295

4H leukodystrophy

POLR-related leukodystrophy

ORPHA:289494

Dermatoleukodystrophy

Cutis laxa-leukodystrophy

ORPHA:1659

Leigh syndrome with leukodystrophy

Infantile subacute necrotizing encephalopathy with leukodystrophy · Leigh disease with leukodystrophy

ORPHA:255241

Leukodystrophy

ORPHA:68356

Oligodontia

Selective tooth agenesis

ORPHA:99798

Ovarioleukodystrophy

ORPHA:99853