Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

5 matching diseasesClear search ×

Corpus callosum agenesis-macrocephaly-hypertelorism syndrome

7q36.3 microduplication syndrome · Dup(7)(q36.3)

ORPHA:459074

3q26 microduplication syndrome

Dup(3)(q26) · Trisomy 3q26

ORPHA:96095

5q35 microduplication syndrome

Dup(5)(q35) · Trisomy 5q35

ORPHA:228415

7q11.23 microduplication syndrome

Dup(7)(q11.23) · Trisomy 7q11.23

ORPHA:96121

Xq12-q13.3 duplication syndrome

Dup(X)(q12-q13.3) · Kaya-Prontera syndrome

ORPHA:314389