Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

6 matching diseasesClear search ×

Juvenile myasthenia gravis

Childhood myasthenia gravis · Generalized myasthenia gravis

ORPHA:391497

Adult-onset myasthenia gravis

Adult-onset acquired myasthenia · Adult-onset autoimmune myasthenia gravis

ORPHA:391490

Myasthenia gravis

Acquired myasthenia · Autoimmune myasthenia gravis

ORPHA:589

Pediatric arterial ischemic stroke

Childhood AIS · Childhood arterial ischemic stroke

ORPHA:439175

Rippling muscle disease with myasthenia gravis

Acquired rippling muscle disease · Generalized myasthenia gravis

ORPHA:206575

Transient neonatal myasthenia gravis

Generalized myasthenia gravis · MG

ORPHA:391504