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Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.
Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"
Congenital muscular dystrophy with cerebellar involvement
CMD with cerebellar involvement · CMD-CRB
Congenital muscular dystrophy
CMD · MDC
Congenital muscular dystrophy due to LMNA mutation
L-CMD · LMNA-related congenital muscular dystrophy
Congenital muscular dystrophy with intellectual disability
CMD with intellectual disability · CMD-MR