Rare Disease Library

Browse Orphanet-curated rare diseases with HPO phenotype annotations, synonyms, and linked support programs. Search by name, abbreviation, or synonym.

Try: "IgA nephropathy", "C3G", "Berger's disease", "PKU", "Duchenne"

5 matching diseasesClear search ×

Esophageal atresia

CEA · Congenital esophageal atresia

ORPHA:1199

Chronic enteropathy associated with SLCO2A1 gene

CEAS

ORPHA:468641

Isolated spontaneous cervical artery dissection

CeAD

ORPHA:689001

Didymosis aplasticosebacea

Aplasia cutis congenita-nevus sebaceus syndrome

ORPHA:370046

Renal caliceal diverticuli-deafness syndrome

Renal caliceal diverticuli-hearing loss syndrome

ORPHA:2838