STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:502434OMIM:617635Q87.0
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome is a rare genetic condition caused by changes (mutations) in the STAG1 gene. This gene plays an important role in how cells divide and how the brain develops before and after birth. Because of this, people with the condition often have intellectual disability, meaning they may learn more slowly and need extra support with thinking, communication, and daily tasks. The condition affects several parts of the body at once. Most people have distinctive facial features that doctors can recognize, along with gastroesophageal reflux disease (GERD), which is when stomach acid flows back up into the food pipe, causing discomfort or feeding problems. Other common features include delayed development of speech and movement, behavioral challenges, and sometimes seizures. There is currently no cure for STAG1-related syndrome. Treatment focuses on managing each symptom — for example, medications or dietary changes for reflux, speech and occupational therapy for developmental delays, and anti-seizure medications if needed. Early intervention and ongoing support from a team of specialists can make a meaningful difference in quality of life. This condition is also sometimes referred to as STAG1 syndrome or STAG1-related neurodevelopmental disorder.

Key symptoms:

Intellectual disability (difficulty with learning and thinking)Delayed speech and language developmentDelayed motor milestones such as sitting and walkingGastroesophageal reflux (stomach acid backing up into the food pipe)Distinctive facial features recognized by doctorsBehavioral challenges such as hyperactivity or anxietySeizures in some individualsFeeding difficulties, especially in infancyShort statureMild to moderate muscle weakness or low muscle tone

Clinical phenotype terms (38)— hover any for plain English
Thin eyebrowHP:0045074Hypoplastic male external genitaliaHP:0000050
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome.

View clinical trials →

No actively recruiting trials found for STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome community →

No specialists are currently listed for STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndromeForum →

No community posts yet. Be the first to share your experience with STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome.

Start the conversation →

Latest news about STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome

No recent news articles for STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type of STAG1 mutation does my child have, and what does that mean for their outlook?,What therapies should we start right away, and how often should they happen?,How should we manage the reflux, and when should we consider changing the treatment?,What signs of seizures should we watch for, and what should we do if one happens?,Are there any clinical trials or research studies we could join?,What kind of educational support will my child need, and how do we access it?,Should other family members be tested for STAG1 changes?

Common questions about STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome

What is STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome?

STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome is a rare genetic condition caused by changes (mutations) in the STAG1 gene. This gene plays an important role in how cells divide and how the brain develops before and after birth. Because of this, people with the condition often have intellectual disability, meaning they may learn more slowly and need extra support with thinking, communication, and daily tasks. The condition affects several parts of the body at once. Most people have distinctive facial features that doctors can recognize, along with ga

How is STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome inherited?

STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome typically begin?

Typical onset of STAG1-related intellectual disability-facial dysmorphism-gastroesophageal reflux syndrome is infantile. Age of onset can vary across affected individuals.