Wiedemann-Steiner syndrome

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:319182OMIM:605130Q87.1
Who is this for?
Show terms as
8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Wiedemann-Steiner syndrome (WSS) is a rare genetic condition that affects many parts of the body. It is caused by changes (mutations) in the KMT2A gene, which plays an important role in how genes are turned on and off during development. The syndrome was first described by doctors Wiedemann and Steiner, and it is sometimes referred to by the abbreviation WSS. People with Wiedemann-Steiner syndrome typically have intellectual disability that ranges from mild to moderate, delayed development (such as late walking or talking), short stature, and distinctive facial features. These facial features may include thick eyebrows, long eyelashes, wide-set eyes, a broad nasal bridge, and a thin upper lip. A hallmark feature is excessive hair growth (hypertrichosis), especially on the elbows, though this is not present in every person. Some individuals may also have low muscle tone, feeding difficulties in infancy, and behavioral challenges. There is currently no cure for Wiedemann-Steiner syndrome. Treatment focuses on managing individual symptoms and supporting development. This may include speech therapy, occupational therapy, physical therapy, and special education services. Early intervention programs can make a meaningful difference in a child's progress. Regular follow-up with a team of specialists helps ensure that medical issues such as heart defects, vision problems, or skeletal differences are identified and treated promptly.

Also known as:

Key symptoms:

Intellectual disability (mild to moderate)Delayed speech and language developmentDelayed motor milestones like walkingShort statureLow muscle tone (feeling floppy)Excessive hair growth, especially on the elbowsThick eyebrows and long eyelashesWide-set eyesBroad or flat nasal bridgeFeeding difficulties in infancyBehavioral challenges such as anxiety or ADHD-like symptomsSmall hands and feetConstipationVision problems such as lazy eye or farsightednessOccasional heart defects

Clinical phenotype terms (50)— hover any for plain English
Low frustration toleranceHP:0000744
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Wiedemann-Steiner syndrome.

View clinical trials →

No actively recruiting trials found for Wiedemann-Steiner syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Wiedemann-Steiner syndrome community →

No specialists are currently listed for Wiedemann-Steiner syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Wiedemann-Steiner syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Wiedemann-Steiner syndromeForum →

No community posts yet. Be the first to share your experience with Wiedemann-Steiner syndrome.

Start the conversation →

Latest news about Wiedemann-Steiner syndrome

No recent news articles for Wiedemann-Steiner syndrome.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific KMT2A mutation does my child have, and does it tell us anything about what to expect?,What therapies should we start right away, and how often should they occur?,Should my child have a heart evaluation or other organ screening?,What educational supports and accommodations should we request at school?,Is there a risk that future children could also have this condition?,Are there any clinical trials or research studies we should know about?,What specialists should be part of my child's care team, and how often should we see them?

Common questions about Wiedemann-Steiner syndrome

What is Wiedemann-Steiner syndrome?

Wiedemann-Steiner syndrome (WSS) is a rare genetic condition that affects many parts of the body. It is caused by changes (mutations) in the KMT2A gene, which plays an important role in how genes are turned on and off during development. The syndrome was first described by doctors Wiedemann and Steiner, and it is sometimes referred to by the abbreviation WSS. People with Wiedemann-Steiner syndrome typically have intellectual disability that ranges from mild to moderate, delayed development (such as late walking or talking), short stature, and distinctive facial features. These facial features

How is Wiedemann-Steiner syndrome inherited?

Wiedemann-Steiner syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Wiedemann-Steiner syndrome typically begin?

Typical onset of Wiedemann-Steiner syndrome is infantile. Age of onset can vary across affected individuals.