Spinal atrophy-ophthalmoplegia-pyramidal syndrome

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Overview

Spinal atrophy-ophthalmoplegia-pyramidal syndrome is an extremely rare neurological condition that combines three main features: spinal muscular atrophy (wasting and weakness of muscles due to nerve cell loss in the spinal cord), ophthalmoplegia (weakness or paralysis of the eye muscles that control eye movement), and pyramidal signs (problems with the nerve pathways that control voluntary movement, leading to stiffness, exaggerated reflexes, and difficulty with coordinated movement). This syndrome falls under the broader category of motor neuron diseases, which are conditions where the nerve cells that control muscles gradually break down and die. Patients with this condition typically experience progressive muscle weakness that can affect the arms and legs, difficulty moving the eyes in various directions, and signs of upper motor neuron involvement such as increased muscle tone and brisk reflexes. The combination of both lower motor neuron signs (muscle wasting and weakness) and upper motor neuron signs (spasticity and hyperreflexia) along with eye movement problems makes this syndrome distinctive. Because this condition is so rare, there is very limited information about its full natural history. There are no specific approved treatments that target the underlying cause. Management is primarily supportive and symptomatic, focusing on physical therapy, occupational therapy, and addressing complications as they arise. A multidisciplinary team of specialists is typically needed to manage the various aspects of this complex condition.

Also known as:

Key symptoms:

Progressive muscle weakness in the arms and legsMuscle wasting (muscles becoming thinner over time)Difficulty moving the eyes or paralysis of eye musclesDouble visionMuscle stiffness or spasticityExaggerated reflexesDifficulty walking or unsteady gaitDrooping eyelidsDifficulty with fine motor tasks like writing or buttoning clothesMuscle twitching or fasciculationsDifficulty swallowing in some casesFatigue

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Spinal atrophy-ophthalmoplegia-pyramidal syndrome.

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No actively recruiting trials found for Spinal atrophy-ophthalmoplegia-pyramidal syndrome at this time.

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Search ClinicalTrials.gov ↗Join the Spinal atrophy-ophthalmoplegia-pyramidal syndrome community →

No specialists are currently listed for Spinal atrophy-ophthalmoplegia-pyramidal syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Spinal atrophy-ophthalmoplegia-pyramidal syndrome.

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Community

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the expected rate of progression for my specific case?,Are there any genetic tests that could help identify the exact cause of my condition?,What therapies or exercises can help me maintain my strength and mobility for as long as possible?,How often should I have my breathing and swallowing function checked?,Are there any clinical trials or research studies I might be eligible for?,What medications can help manage my spasticity or other symptoms?,Should my family members be tested for this condition?

Common questions about Spinal atrophy-ophthalmoplegia-pyramidal syndrome

What is Spinal atrophy-ophthalmoplegia-pyramidal syndrome?

Spinal atrophy-ophthalmoplegia-pyramidal syndrome is an extremely rare neurological condition that combines three main features: spinal muscular atrophy (wasting and weakness of muscles due to nerve cell loss in the spinal cord), ophthalmoplegia (weakness or paralysis of the eye muscles that control eye movement), and pyramidal signs (problems with the nerve pathways that control voluntary movement, leading to stiffness, exaggerated reflexes, and difficulty with coordinated movement). This syndrome falls under the broader category of motor neuron diseases, which are conditions where the nerve