Rare pediatric systemic disease

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ORPHA:280373
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1Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Rare pediatric systemic disease (Orphanet code 280373) is a broad classification term used in medical databases to group uncommon conditions that affect multiple organ systems in children. Because this is a grouping category rather than a single specific disease, it encompasses a range of disorders that can involve the immune system, blood vessels, connective tissues, and other organs throughout the body. Children with these conditions may experience symptoms that affect many parts of the body at the same time, which can make diagnosis challenging. Symptoms vary widely depending on the specific underlying condition but often include persistent fevers, skin rashes, joint pain or swelling, fatigue, and problems with internal organs such as the kidneys, liver, or lungs. Some children may also have growth delays or developmental concerns. Because these diseases affect the whole body, they typically require care from multiple specialists working together. The treatment landscape for rare pediatric systemic diseases has improved in recent years, with advances in genetic testing helping doctors reach diagnoses faster. Treatments range from medications that calm the immune system (such as corticosteroids and biologic therapies) to supportive care addressing specific organ involvement. Early diagnosis and a coordinated care team are essential for the best possible outcomes.

Key symptoms:

Persistent or recurring feversSkin rashesJoint pain or swellingExtreme tiredness or fatigueUnexplained weight lossSwollen lymph nodesOrgan inflammation (kidneys, liver, lungs)Growth delaysMuscle weakness or painEye redness or vision changesMouth soresAbdominal painDifficulty breathing

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Childhood

Begins in childhood, roughly ages 1 to 12

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Rare pediatric systemic disease.

View clinical trials →

No actively recruiting trials found for Rare pediatric systemic disease at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Rare pediatric systemic disease community →

Specialists

1 foundView all specialists →
NR
Nilsa Ramirez
COLUMBUS, OH
Specialist
PI on 1 active trial16 Rare pediatric systemic disease publications

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Rare pediatric systemic disease.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Rare pediatric systemic diseaseForum →

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Latest news about Rare pediatric systemic disease

No recent news articles for Rare pediatric systemic disease.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific diagnosis does my child have within the category of rare pediatric systemic diseases?,Which organs are affected, and how will you monitor them over time?,What are the treatment options, and what are the potential side effects?,Should my child have genetic testing, and what might the results mean for our family?,What signs or symptoms should prompt me to seek emergency care?,Are there any clinical trials or new treatments available for my child's condition?,What support services are available to help my child at school and in daily life?

Common questions about Rare pediatric systemic disease

What is Rare pediatric systemic disease?

Rare pediatric systemic disease (Orphanet code 280373) is a broad classification term used in medical databases to group uncommon conditions that affect multiple organ systems in children. Because this is a grouping category rather than a single specific disease, it encompasses a range of disorders that can involve the immune system, blood vessels, connective tissues, and other organs throughout the body. Children with these conditions may experience symptoms that affect many parts of the body at the same time, which can make diagnosis challenging. Symptoms vary widely depending on the specif

At what age does Rare pediatric systemic disease typically begin?

Typical onset of Rare pediatric systemic disease is childhood. Age of onset can vary across affected individuals.

Which specialists treat Rare pediatric systemic disease?

1 specialists and care centers treating Rare pediatric systemic disease are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.