Primary hyperaldosteronism-seizures-neurological abnormalities syndrome

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ORPHA:369929OMIM:615474E26.0
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1Specialists8Treatment centers

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Overview

Primary hyperaldosteronism-seizures-neurological abnormalities syndrome (also known as PASNA syndrome) is an extremely rare genetic condition that affects both the adrenal glands and the brain. The disease is caused by mutations in the CACNA1D gene, which provides instructions for making a type of calcium channel found in many tissues throughout the body, including the adrenal glands and the nervous system. In this condition, the adrenal glands produce too much of a hormone called aldosterone. Aldosterone normally helps control blood pressure and the balance of salt and water in the body. When too much aldosterone is made, it can lead to high blood pressure and low potassium levels. At the same time, the brain is also affected, leading to seizures (epilepsy) and other neurological problems such as developmental delays, movement difficulties, and sometimes cerebral palsy-like features. Because this syndrome affects multiple body systems, treatment requires a team of specialists. Managing the excess aldosterone may involve medications that block its effects, such as mineralocorticoid receptor antagonists (like spironolactone or eplerenone). Seizures are treated with anti-epileptic medications. There is currently no cure, and treatment focuses on managing symptoms and preventing complications like dangerously high blood pressure or uncontrolled seizures.

Key symptoms:

High blood pressure, sometimes severeSeizures or epilepsyLow potassium levels in the bloodDevelopmental delayMuscle stiffness or spasticityDifficulty with movement and coordinationIntellectual disabilityAbnormal involuntary movementsCerebral palsy-like symptomsExcessive aldosterone productionFailure to thrive in infancyDifficulty feeding as a babyHeart rhythm problems

Clinical phenotype terms (30)— hover any for plain English
Increased circulating aldosterone concentrationHP:0000859Abnormal circulating renin concentrationHP:0040084Ventricular hypertrophyHP:0001714AthetosisHP:0002305Focal myoclonic seizureHP:0011166Caesarean sectionHP:0011410Second degree atrioventricular blockHP:0011706EMG: impaired neuromuscular transmissionHP:0100285
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Primary hyperaldosteronism-seizures-neurological abnormalities syndrome.

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No actively recruiting trials found for Primary hyperaldosteronism-seizures-neurological abnormalities syndrome at this time.

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Specialists

1 foundView all specialists →
CP
Chi Hornik, PharmD
DURHAM, NC
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Primary hyperaldosteronism-seizures-neurological abnormalities syndrome.

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Caregiver Resources

NORD Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.What specific CACNA1D mutation does my child have, and what does it mean for their prognosis?,What medications are best for controlling both the high blood pressure and the seizures?,How often should blood pressure and potassium levels be checked?,Are there any experimental or targeted therapies being studied for this condition?,What therapies (physical, occupational, speech) should we start, and how often?,What should I do if my child has a prolonged seizure at home?,Should other family members be tested for this genetic change?

Common questions about Primary hyperaldosteronism-seizures-neurological abnormalities syndrome

What is Primary hyperaldosteronism-seizures-neurological abnormalities syndrome?

Primary hyperaldosteronism-seizures-neurological abnormalities syndrome (also known as PASNA syndrome) is an extremely rare genetic condition that affects both the adrenal glands and the brain. The disease is caused by mutations in the CACNA1D gene, which provides instructions for making a type of calcium channel found in many tissues throughout the body, including the adrenal glands and the nervous system. In this condition, the adrenal glands produce too much of a hormone called aldosterone. Aldosterone normally helps control blood pressure and the balance of salt and water in the body. Whe

How is Primary hyperaldosteronism-seizures-neurological abnormalities syndrome inherited?

Primary hyperaldosteronism-seizures-neurological abnormalities syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Primary hyperaldosteronism-seizures-neurological abnormalities syndrome typically begin?

Typical onset of Primary hyperaldosteronism-seizures-neurological abnormalities syndrome is neonatal. Age of onset can vary across affected individuals.

Which specialists treat Primary hyperaldosteronism-seizures-neurological abnormalities syndrome?

1 specialists and care centers treating Primary hyperaldosteronism-seizures-neurological abnormalities syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.